Research

Our focus is to raise awareness of the latest research into sickle cell disease.

Gene Editing

CRISPR (clustered regularly interspaced short palindromic repeats) – this is bacteria’s antiviral mechanism Cas9 – an enzyme that cuts DNA || Guide RNA (mRNA – messenger RNA)

The editing tool (CRISPR) is used to disable the BCL11A gene which shuts down the production of foetal haemoglobin (HbF)

                                                                        Clinical Trials

Clinical trials of new therapeutic drugs and blood cell exchange equipment. New treatment protocols and non-opioid interventions. We will be partnering with bio-pharmaceutical companies creating therapeutic treatments for SCD. 

 

Registers

https://clinicaltrials.gov/ct2/home                                                                                          https://www.nih.gov/health-information/nih-clinical-research-trials-you

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